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Therapeutic Areas

Rare Disease Commercialization and Marketing Solutions

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Rare disease therapies face a distinct set of access challenges, including low-prevalence populations, diagnostic delays, and highly specialized care pathways.

Adding to the challenge, access strategies often need to commence six months or more ahead of a BLA (Biologics License Application) filing. Continuity from early engagement through launch is essential to achieving policy alignment and timely access.

How can we support your rare disease therapy?

 At TJP, we help clients overcome these challenges with strategies designed to educate the market, empower diagnosis, and drive sustainable adoption. We understand how to provide tailored patient services, from initial diagnostic support to long-term continuity of care.

Execute a strategic rare disease launch

Rare disease therapies face heightened scrutiny from payers, limited clinical data sets, and small patient populations that complicate traditional commercialization playbooks. Success demands a strategic approach from day one.

We align patient access, marketing, and market access strategies to ensure every touchpoint reinforces a cohesive, compelling value story.
Experience

Experience supporting commercialization efforts for ultra-rare and orphan indications with highly specialized care pathways

Guidance

Guidance on early payer engagement for breakthrough or accelerated therapies, including pre-approval efforts to educate on clinical value and unmet needs

Strategic

Strategic frameworks that account for diagnostic delays, limited prescriber experience, and the influence of Centers of Excellence

support

Full-spectrum support from pre-launch strategy through post-launch pull-through and ongoing access optimization

feedback

Nuanced feedback from the TJP Market Access Council, an expert team established for strategy consultation and marketing material evaluation

Rare disease market

Rare disease market access solutions informed by real-world complexities

TJP develops strategies that reflect the challenging dynamics of rare disease care, from the complexity of securing coverage for novel and orphan therapies to the logistical challenges patients face accessing treatment. Our data-driven outreach is designed to meet payer expectations for real-world evidence across the extended timelines required to demonstrate value in ultra-rare conditions.

We build credibility with HCPs and patient communities through messaging that reflects lived experience, addresses diagnostic uncertainty, and reinforces long-term commitment to rare conditions. 

Site-of-care dynamics in rare diseases often involve specialized academic centers or Centers of Excellence (CoEs), which introduce unique onboarding, referral, and treatment logistics. To navigate multi-step diagnoses and coverage pathways, we help teams build execution-ready tools like referral form templates, draft coverage appeal letters, CoE onboarding guides, and patient-facing documentation.

Full-service support for multi-channel rare disease therapy marketing

Effective marketing of rare disease therapies must engage niche stakeholders through data-rich content delivered through carefully targeted omnichannel strategies. Every touchpoint, from provider education materials to caregiver empowerment, contributes to long-term market success. We help clients develop and execute coordinated strategies that:
1
Build credible brand platforms rooted in evidence for genetic, metabolic, and ultra-rare condition therapies.
2

Equip field teams and specialty reps with tools to engage physicians, patient advocacy groups, and Centers of Excellence.

3

Integrate digital, live, and peer-driven channels to inform decisions, activate advocates, and nurture support.

Rare Disease Novel Therapy Commercialization Success Story

We helped a novel therapy for Duchennes Muscular Dystrophy (DMD) address treatment delays that were hampering access, successfully reducing initial time-to-fill rate and delay in therapy by 27 days.
immunology therapy

How can we help drive access wins for your rare disease therapy?

From initial access planning to long-term pull-through, we help teams navigate the complexity of rare disease markets with precision and empathy. Our approach melds strategic insight and hands-on support to help your therapy reach the patients who need it most.

Let us know how we can help.